This study investigates the experiences of individuals with stage 2 Type 1 diabetes in the United States. The study compares those who have received an infusion with an investigational medication and those who have not.Participants will provide information on their quality of life, diabetes-related anxiety, and how they manage their …
This study investigates atopic dermatitis (AD) in adolescents and adults. The purpose is to understand the unmet needs of patients with AD and evaluate the safety and effectiveness of systemic treatments in real-world settings. The study will also examine factors like age, skin color, triggers for AD flares, and other …
This study investigates the long-term outcomes of individuals with various non-cancerous blood disorders, including hemophilia, von Willebrand Disease, and congenital platelet disorders. The purpose is to collect comprehensive data on the safety and effectiveness of treatments over an extended period. The study is observational, meaning it tracks participants as they …
This study investigates the effects of atopic dermatitis (AD) on pregnancy outcomes. This observational study will compare the incidence of adverse pregnancy outcomes, such as miscarriage or stillbirth, and the prevalence of adverse infant outcomes, like major congenital malformations or being small for gestational age, in women with AD who …
This study investigates Fabry disease, a rare genetic disorder. The purpose of this study is to track the routine clinical outcomes for patients with Fabry disease, without altering their treatment. This is an observational study, meaning that data is collected by observing participants receiving routine care, without changing their treatment, …
This study investigates the clinical outcomes of patients with Gaucher disease through an observational registry. The purpose of the registry is to gather data on how the disease progresses and affects patients over time, without altering their treatment plans. This helps in understanding the natural history of the disease and …
This study investigates the effects of exposure to an investigational vaccine during pregnancy. The purpose is to assess maternal, obstetrical, pregnancy, neonatal, and infant outcomes among women who were vaccinated with the investigational vaccine during pregnancy or in the 30 days before their last menstrual period.Participants in this observational study …
This study investigates the safety of an investigational medication when used by women during pregnancy and/or lactation. The purpose is to assess any risks associated with the investigational medication on pregnancy, as well as potential complications and adverse effects in the developing fetus, neonate, and infant.Participants will have their data …
This study investigates the long-term safety and immune response to an investigational therapy in children under 2 years old with a condition called Acid Sphingomyelinase Deficiency (ASMD). The purpose of this study is to observe how the investigational therapy affects children with this condition over time.Participants in the study will …
This study investigates Stage 2 Type 1 Diabetes (T1D), focusing on abnormal blood sugar control without symptoms. The study involves collecting general information on patients with Stage 2 T1D and observing the long-term effects of a specific investigational medication. Participants will be divided into two study arms: those exposed to …
