This study investigates the effects of atopic dermatitis (AD) on pregnancy outcomes. This observational study will compare the incidence of adverse pregnancy outcomes, such as miscarriage or stillbirth, and the prevalence of adverse infant outcomes, like major congenital malformations or being small for gestational age, in women with AD who …
This study investigates the effects and outcomes of systemic treatments in patients with atopic dermatitis (AD). The purpose of this study is to understand the patient journey and assess the safety and clinical outcomes of these treatments in a real-world setting. Atopic dermatitis can vary in severity, and systemic treatments …
This study investigates Fabry disease and its impact on pregnancy outcomes. The purpose of this observational study is to track the clinical outcomes of patients with Fabry disease, including those who are pregnant, to better understand the disease's progression and variability.Participants will undergo routine clinical assessments and receive standard care …
This study investigates Pompe disease, focusing on muscle function impacts due to glycogen buildup. The purpose of this observational study is to track the natural history and outcomes of Pompe disease in patients worldwide, regardless of treatment status. An observational study involves collecting data by observing participants receiving routine care, …
This study investigates the long-term safety and effectiveness of therapies for non-neoplastic hematologic disorders. The purpose is to collect data from participants with various blood disorders, such as hemophilia, von Willebrand Disease, and congenital platelet disorders, over a period of at least 15 years. Participants will be grouped into specific …
This study investigates pregnancy outcomes in women with Pompe disease. The study is observational, meaning it involves monitoring and collecting data on pregnant women with Pompe disease, whether or not they are receiving enzyme replacement therapy (ERT) or other treatments. The aim is to gather information on pregnancy complications and …
This study investigates the effects of exposure to an investigational vaccine during pregnancy. The purpose is to assess maternal, obstetrical, pregnancy, neonatal, and infant outcomes among women who were vaccinated with the investigational vaccine during pregnancy or in the 30 days before their last menstrual period.Participants in this observational study …
This study investigates the long-term safety and immune response to an investigational therapy in children under 2 years old with a condition called Acid Sphingomyelinase Deficiency (ASMD). The purpose of this study is to observe how the investigational therapy affects children with this condition over time.Participants in the study will …
This study investigates Stage 2 Type 1 Diabetes (T1D), focusing on abnormal blood sugar control without symptoms. The study involves collecting general information on patients with Stage 2 T1D and observing the long-term effects of a specific investigational medication. Participants will be divided into two study arms: those exposed to …
This study investigates pregnancy and infant outcomes in women exposed to an investigational medication during pregnancy. The study compares these outcomes with those of two other groups: pregnant women with similar health conditions who are not exposed to the investigational medication, and healthy pregnant women. The primary focus is on …
