This study investigates Fabry disease and its impact on pregnancy outcomes. The purpose of this observational study is to track the clinical outcomes of patients with Fabry disease, including those who are pregnant, to better understand the disease's progression and variability.Participants will undergo routine clinical assessments and receive standard care …
This study investigates the effects of exposure to an investigational vaccine during pregnancy. The purpose is to assess maternal, obstetrical, pregnancy, neonatal, and infant outcomes among women who were vaccinated with the investigational vaccine during pregnancy or in the 30 days before their last menstrual period.Participants in this observational study …
This study investigates the long-term safety and immune response to an investigational therapy in children under 2 years old with a condition called Acid Sphingomyelinase Deficiency (ASMD). The purpose of this study is to observe how the investigational therapy affects children with this condition over time.Participants in the study will …
This study investigates pregnancy and infant outcomes in women exposed to an investigational medication during pregnancy. The study compares these outcomes with those of two other groups: pregnant women with similar health conditions who are not exposed to the investigational medication, and healthy pregnant women. The primary focus is on …
This study investigates the safety of an investigational medication when used by women during pregnancy and lactation. The purpose is to collect data on the effects of the medication on pregnancy outcomes, maternal health, and the developing child. Outcomes in infants exposed to the medication will be assessed, including their …
This study investigates the real-world effectiveness and safety of an investigational medication in patients with chronic spontaneous urticaria (CSU). The purpose of this study is to collect data from participants' medical records and patient-reported outcomes to better understand the treatment's impact on disease, work productivity, quality of life, and hospitalizations …
This study investigates Stage 2 Type 1 Diabetes (T1D), focusing on abnormal blood sugar control without symptoms. The study involves collecting general information on patients with Stage 2 T1D and observing the long-term effects of a specific investigational medication. Participants will be divided into two study arms: those exposed to …
