This study investigates the long-term safety and immune response to an investigational therapy in children under 2 years old with a condition called Acid Sphingomyelinase Deficiency (ASMD). The purpose of this study is to observe how the investigational therapy affects children with this condition over time.Participants in the study will …
This study investigates the safety of an investigational medication when used by women during pregnancy and lactation. The purpose is to collect data on the effects of the medication on pregnancy outcomes, maternal health, and the developing child. Outcomes in infants exposed to the medication will be assessed, including their …
This study investigates the real-world effectiveness, safety, and usage patterns of an investigational medication in patients with chronic spontaneous urticaria (CSU). The purpose of the study is to observe how the investigational medication performs in a real-world setting.Participants will have their medical data collected as part of routine care, along …
This study investigates Stage 2 Type 1 Diabetes, focusing on the early stage of the disease where blood sugar levels are abnormal. The purpose of this study is to collect information on patients with Stage 2 Type 1 Diabetes and observe the long-term effects of an investigational medication. Participants will …
