This study investigates the long-term safety and efficacy of an investigational medication in adult participants with asthma. Participants who have completed previous studies with the investigational medication are eligible to join this extended study.Participants will receive the investigational medication and continue their background therapy, which may include inhaled corticosteroids and …
This study investigates the safety and effectiveness of an investigational treatment in adults with Type 2 diabetes. The main purpose of this study is to understand how the investigational treatment works in managing this condition.Participants in the study will receive the investigational treatment, and their health will be monitored through …
This study investigates the clinical outcomes of patients with Gaucher disease through an observational registry. The purpose of the registry is to gather data on how the disease progresses and affects patients over time, without altering their treatment plans. This helps in understanding the natural history of the disease and …
This study investigates Mucopolysaccharidosis I (MPS I), a rare genetic disorder. The purpose of this observational study is to collect data on the natural history and progression of MPS I and to observe clinical responses in patients receiving enzyme replacement therapy or other treatments.Participants in this study will have their …
This study investigates Pompe disease, a rare genetic disorder. The purpose of this observational study is to track the disease's natural history and outcomes in patients, both those receiving treatment and those who are not. An observational study is a type of research study where data is collected by observing …
This study investigates Fabry disease, a rare genetic disorder. The purpose of this study is to track the routine clinical outcomes for patients with Fabry disease, without altering their treatment. This is an observational study, meaning that data is collected by observing participants receiving routine care, without changing their treatment, …
