This study investigates the use of an investigational medication in combination with other treatments for adults who have relapsed or refractory multiple myeloma.The study focuses on evaluating the effectiveness of this combination treatment. Researchers aim to understand how well the treatment works in improving the condition of participants who have …
This study investigates the effectiveness of different investigational medications compared to a placebo in improving lung capacity in participants with Interstitial Lung Disease (ILD) secondary to Systemic Sclerosis (SSc). The purpose is to observe changes from the start to the end of the treatment period at Week 52.Participants in the …
This study investigates the safety and effects of an investigational mRNA vaccine for individuals with mild acne. The study will include two groups, a Sentinel Cohort to initially assess safety, and a Main Cohort for broader evaluation.Participants will receive two administrations of the investigational vaccine. The study will consist of …
This study investigates the safety and effectiveness of a one-time injection for people with Geographic Atrophy related to Age-related Macular Degeneration. The study focuses on assessing how well the investigational injection works and its safety for participants. Researchers aim to gather data on the treatment's impact on vision over time.Who …
This study investigates the safety and ability of an investigational pneumococcal vaccine to help the body develop antibodies in children and adolescents with sickle cell disease. The study is focused on children aged 2 to 17 years, who may or may not have received previous vaccinations against pneumococcal disease.The study …
This study investigates the experiences of adults with relapsed or refractory multiple myeloma. The purpose is to gather data about patients receiving standard care with an investigational medication. Researchers aim to collect various types of data, including quantitative, qualitative, and wearable data, to understand the treatment experience better.Participants will be …
This study investigates the administration of an investigational medication for people with multiple sclerosis (MS). The purpose is to compare two ways of giving the medication: under the skin (subcutaneous) and into the vein (intravenous).The study focuses on understanding how these two methods of administration affect the treatment of MS. …
This study investigates Gaucher disease, a genetic disorder characterized by the accumulation of Gaucher cells in areas like the spleen, liver, and bone marrow. The purpose of this study is to observe patients with Gaucher disease to better understand the condition and its progression.The study focuses on understanding the variability …
This study investigates Pompe disease, a rare genetic disorder. The study focuses on understanding how Pompe disease progresses and varies among individuals. It also aims to evaluate the long-term outcomes of individuals with this condition, whether they receive treatment or not.Who can participate: Individuals of any age with a confirmed …
This study investigates Fabry disease and aims to learn more about its variability, progression, and natural history. The study includes both men and women with Fabry disease and does not involve any experimental treatments. Participants will receive regular medical care as directed by their doctors.The purpose of this study is …
