This study investigates pregnancy outcomes in women with Pompe disease. This study includes women who are pregnant or have been pregnant and are already part of the Pompe Registry.The purpose of this study is to observe and collect data about pregnancy complications and infant growth in women with Pompe disease. …
This study investigates Pompe disease, focusing on gathering information about how the disease progresses over time in patients who are both treated and untreated.The study focuses on understanding the variability and natural history of Pompe disease. It aims to provide insights that can help improve patient care and evaluate the …
This study investigates the safety of an investigational medication when used by women during pregnancy and lactation. The purpose is to collect data on the effects of the medication on pregnancy outcomes, maternal health, and the developing child. Outcomes in infants exposed to the medication will be assessed, including their …
