This study investigates advanced solid tumors in adults. Participants in this study have tumors that are either hard to treat or have spread to other parts of the body, making them unresectable or metastatic.The purpose of this study is to evaluate the safety of an investigational medication in treating these …
This study investigates the clinical outcomes of patients with Gaucher disease. The study is observational, meaning it collects data from patients receiving routine care without altering their treatment. It aims to enhance understanding of the disease's variability, progression, and natural history to aid in better therapeutic interventions.Participants will undergo clinical …
This study investigates Fabry disease, a genetic condition affecting various parts of the body. The purpose is to understand the condition's variability, progression, and natural history in patients, including women who carry the gene.The study focuses on collecting data to improve patient care and to evaluate the safety and effectiveness …
