This study investigates the long-term safety and tolerability of an investigational medication in adults with different forms of multiple sclerosis, including relapsing MS (RMS), primary progressive MS (PPMS), and non-relapsing secondary progressive MS (NRSPMS).Participants in this study will continue to receive the investigational medication in an open-label format, meaning both …
This study investigates advanced solid tumors, focusing on the safety of an investigational medication, a type of antibody-drug conjugate (ADC), in participants with these challenging-to-treat cancers.Participants will take part in a study with five different parts. Parts A and B will focus on determining the appropriate dosage of the investigational …
This study investigates the clinical outcomes of patients with Gaucher disease. The study is observational, meaning it collects data from patients receiving routine care without altering their treatment. It aims to enhance understanding of the disease's variability, progression, and natural history to aid in better therapeutic interventions.Participants will undergo clinical …
This study investigates Fabry disease and its impact on pregnancy outcomes. The purpose of this observational study is to track the clinical outcomes of patients with Fabry disease, including those who are pregnant, to better understand the disease's progression and variability.Participants will undergo routine clinical assessments and receive standard care …
This study investigates Mucopolysaccharidosis I (MPS I), a rare genetic disorder. The purpose of this observational study is to collect data on the natural history and progression of MPS I and to observe clinical responses in patients receiving enzyme replacement therapy or other treatments.Participants in this study will have their …
