This study investigates the condition known as chronic inflammatory demyelinating polyneuropathy (CIDP) in adults who have not responded to usual treatments.The study focuses on evaluating the effectiveness and safety of an investigational medication compared to a placebo in adults with CIDP. It aims to understand whether the investigational medication can …
This study investigates the effects of an investigational medication compared to a placebo in adults with high-risk asthma.The focus of this study is to evaluate the safety, effectiveness, and tolerability of the investigational medication as an add-on therapy. Researchers aim to understand how this treatment works for people who are …
This study investigates the effects of an investigational medication in adults with moderate to severe Crohn's Disease.The purpose of this study is to evaluate the safety and effectiveness of different doses of the investigational medication. Researchers aim to understand how well the medication works in reducing the symptoms associated with …
This study investigates the effects of an investigational treatment on patients with ulcerative colitis. The purpose is to see how well the treatment works and how safe it is for people with moderate-to-severe forms of this condition.The focus of the study is to evaluate the effectiveness and safety of different …
This study investigates the safety and effectiveness of an investigational medication in boys aged 1 to under 12 years who have hemophilia A or B.The purpose of this study is to observe how well the investigational medication works and how safe it is for these young boys. The study will …
This study investigates how effective an investigational medication is for treating chronic lung allograft dysfunction (CLAD) in adults.The study focuses on evaluating the safety and effectiveness of the investigational medication when used alongside standard treatments. It aims to understand if this approach can improve lung function in people with CLAD.Who …
This study investigates the effects of an investigational medication in adults with relapsing forms of multiple sclerosis. The purpose of this study is to evaluate the safety and effectiveness of the investigational medication. Researchers aim to understand its impact on the annualized relapse rate, which measures how often relapses occur …
This study investigates the long-term safety and effectiveness of an investigational medication in adults with asthma.The focus of this study is to observe how well the investigational medication works over an extended period and to monitor any side effects that may occur. The study aims to provide more information about …
This study investigates Gaucher disease, aiming to understand its variability and progression to improve therapeutic interventions.The study also focuses on evaluating pregnancy outcomes in women with Gaucher disease. It aims to track complications and infant growth to enhance patient care.Who can participate: Adults and children with confirmed Gaucher disease can …
This study investigates Pompe disease, a rare genetic disorder. The study focuses on understanding how Pompe disease progresses and varies among individuals. It also aims to evaluate the long-term outcomes of individuals with this condition, whether they receive treatment or not.Who can participate: Individuals of any age with a confirmed …
