This study investigates the effects of an investigational medication in adults with high-risk asthma. The purpose of this study is to learn more about how this medication might work for people with asthma who cannot use biologic treatments.The study will evaluate the safety, effectiveness, and tolerability of the investigational medication. …
This study investigates the effects of an investigational medication on adults with moderate to severe Crohn's Disease.The purpose of this study is to evaluate the safety and effectiveness of the investigational medication in managing symptoms of Crohn's Disease. Researchers aim to understand how different doses impact the condition over time.Who …
This study investigates the effects of an investigational medication on individuals with moderate-to-severe ulcerative colitis.The study aims to evaluate the safety and effectiveness of different doses of the investigational medication in achieving clinical remission in patients. Researchers are particularly interested in understanding how well the medication works and its safety …
This study investigates the efficacy and safety of an investigational medication in young boys with hemophilia A or B. The study focuses on boys aged 1 to less than 12 years who have severe forms of this condition.The purpose of this study is to evaluate how well the investigational medication …
This study investigates the safety and efficacy of an investigational medication in people aged 12 and older with moderate to severe atopic dermatitis.The focus of this study is to evaluate how safe and effective the investigational medication is over a long period. The study aims to understand better how the …
This study investigates relapsing forms of multiple sclerosis. The purpose of this study is to measure the annualized relapse rate in adults with this condition.The study will focus on evaluating the safety and effectiveness of an investigational medication compared to an existing treatment. It aims to provide insights into how …
This study investigates the long-term safety and efficacy of an investigational medication in adults with asthma. It is an extension of previous studies and will last up to 100 weeks, with participants receiving treatment for up to 96 weeks. The purpose of this study is to continue monitoring the effects …
This study investigates the clinical outcomes of patients with Gaucher disease. The study is observational, meaning it collects data from patients receiving routine care without altering their treatment. It aims to enhance understanding of the disease's variability, progression, and natural history to aid in better therapeutic interventions.Participants will undergo clinical …
This study investigates Pompe disease, focusing on muscle function impacts due to glycogen buildup. The purpose of this observational study is to track the natural history and outcomes of Pompe disease in patients worldwide, regardless of treatment status. An observational study involves collecting data by observing participants receiving routine care, …
This study investigates Fabry disease, a genetic condition affecting various parts of the body. The purpose is to understand the condition's variability, progression, and natural history in patients, including women who carry the gene.The study focuses on collecting data to improve patient care and to evaluate the safety and effectiveness …
