This study investigates the efficacy and safety of an investigational medication in people with sickle-cell disease.The focus of this study is to evaluate how well the investigational medication works and how safe it is for participants with sickle-cell disease.Who can participate: Participants aged 10 to 65 years with diagnosed sickle-cell …
This study investigates the safety and ability of an investigational pneumococcal vaccine to stimulate the immune system in children and adolescents with sickle cell disease. Participants will receive either the investigational vaccine or a licensed pneumococcal vaccine, and researchers will compare the immune response between the two groups.Participants in the …
This study investigates the long-term safety and effectiveness of therapies for non-neoplastic hematologic disorders. The purpose is to collect data from participants with various blood disorders, such as hemophilia, von Willebrand Disease, and congenital platelet disorders, over a period of at least 15 years. Participants will be grouped into specific …
